NCT05609162 2022-12-15
TBMPPF
Sun Yat-sen University
Unknown
Sun Yat-sen University
SynerGene Therapeutics, Inc.
Peking Union Medical College Hospital
Centre Leon Berard
Beijing Tiantan Hospital
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
Huazhong University of Science and Technology
Office of Rare Diseases (ORD)