Clinical Trials Browser

Interventional × Congenital Bone Marrow Failure Syndromes × Classical hematology × Clear all

Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Cytopenia, Neoplastic Syndromes, Hereditary, Hematologic Neoplasms

NCT07408583 2026-02-19

Prenatal Transplantation for Fetuses With Fanconi Anemia

Phase 1/2 Not yet recruiting

12 enrolled

Classical hematology

Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Fanconi Anemia, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Anemia, Hypoplastic, Congenital, Genetic Diseases, Inborn, DNA Repair-Deficiency Disorders

NCT06090669 2026-02-17

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

Phase 1 Recruiting

75 enrolled

Classical hematology

Congenital Bone Marrow Failure Syndromes

NCT06839456 2025-03-25

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Phase 1/2 Recruiting

100 enrolled

Classical hematologyLymphoidOther hematologic neoplasm

Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Anemia, Refractory, with Excess of Blasts, Hemoglobinopathies, Immunologic Deficiency Syndromes, Leukemia, Lymphoma, Non-Hodgkin, Metabolism, Inborn Errors

Clinical Trials

Pre-myeloid Cancer and Bone Marrow Failure Clinic Study

Prenatal Transplantation for Fetuses With Fanconi Anemia

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT