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Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Cytopenia, Neoplastic Syndromes, Hereditary, Hematologic Neoplasms

NCT06090669 2026-02-17

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

Phase 1 Recruiting

75 enrolled

Classical hematology

Congenital Bone Marrow Failure Syndromes

NCT06839456 2025-03-25

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Phase 1/2 Recruiting

100 enrolled

Classical hematologyLymphoidOther hematologic neoplasm

Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Anemia, Refractory, with Excess of Blasts, Hemoglobinopathies, Immunologic Deficiency Syndromes, Leukemia, Lymphoma, Non-Hodgkin, Metabolism, Inborn Errors

Clinical Trials

Pre-myeloid Cancer and Bone Marrow Failure Clinic Study

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT