OTHER × Genetic Diseases, Inborn × Clear all
NCT04880356 2024-11-19

Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.

Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta

Recruiting
100 enrolled
NCT01200017 2021-05-27

Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell Transplant

University of California, San Francisco

No longer available