NCT07218575 2025-10-20Double-Blind Trial of Everolimus for Improving Social Abilities in PTEN Germline MutationsBoston Children's HospitalPhase 2/3 Not yet recruiting60 enrolled
NCT02991807 2025-02-17RAD001 and Neurocognition in PTEN Hamartoma Tumor SyndromeBoston Children's HospitalPhase 1/2 Completed46 enrolled 15 charts