Clinical Trials

1 trials
RecentStart dateEnrollment
Observational × Metabolism, Inborn Errors × Clear all
NCT00005900 2005-06-24

Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation

Office of Rare Diseases (ORD)

Unknown
10 enrolled

Adrenoleukodystrophy, Fucosidosis, Gaucher Disease, Leukodystrophy, Globoid Cell, Leukodystrophy, Metachromatic, Mucopolysaccharidosis I, Metabolism, Inborn Errors, Mucolipidoses, Mucopolysaccharidoses, Mucopolysaccharidosis VI, Niemann-Pick Diseases, Sphingolipidoses, Wolman Disease, Genetic Diseases, Inborn, Rare Diseases, Mannosidase Deficiency Diseases