NCT02991807 2025-02-17RAD001 and Neurocognition in PTEN Hamartoma Tumor SyndromeBoston Children's HospitalPhase 1/2 Completed46 enrolled 15 charts
NCT00971789 2015-09-30Sirolimus to Treat Cowden Syndrome and Other PTEN Hamartomatous Tumor SyndromesNational Institutes of Health Clinical Center (CC)Phase 2 Completed18 enrolled 7 charts