Clinical Trials

Amyotrophic Lateral Sclerosis, Charcot-Marie-Tooth Disease, Glycogen Storage Disease Type II, Muscular Atrophy, Spinal, Myasthenia Gravis, Neuromuscular Diseases, Spastic Paraplegia, Hereditary, Lambert-Eaton Myasthenic Syndrome, Postpoliomyelitis Syndrome, Motor Neuron Disease, Mitochondrial Myopathies, Myopathies, Nemaline, Myositis, Inclusion Body, Polyradiculoneuropathy, Chronic Inflammatory Demyelinating, Muscular Dystrophy, Facioscapulohumeral, Myopathies, Structural, Congenital, Postural Orthostatic Tachycardia Syndrome

Amyotrophic Lateral Sclerosis, Friedreich Ataxia, Glycogen Storage Disease Type II, Muscular Atrophy, Spinal, Myasthenia Gravis, Myotonic Dystrophy, Neuromuscular Diseases, Hereditary Sensory and Motor Neuropathy, Lambert-Eaton Myasthenic Syndrome, Myositis, Inclusion Body, Guillain-Barre Syndrome, Polyradiculoneuropathy, Chronic Inflammatory Demyelinating, Muscular Dystrophy, Facioscapulohumeral

Friedreich Ataxia, Glycogen Storage Disease Type II, Muscular Atrophy, Spinal, Myotonic Dystrophy, Neuromuscular Diseases, Hereditary Sensory and Motor Neuropathy, Lambert-Eaton Myasthenic Syndrome, Myositis, Inclusion Body, Guillain-Barre Syndrome, Polyradiculoneuropathy, Chronic Inflammatory Demyelinating, Muscular Dystrophy, Facioscapulohumeral, Muscular Dystrophies, Limb-Girdle

Endocrine System Diseases, Muscular Atrophy, Spinal

Infertility, Muscular Atrophy, Spinal, Multiple Endocrine Neoplasia Type 1

Colonic Neoplasms, Muscular Atrophy, Spinal, Hyperbilirubinemia, Neonatal